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Disease Classifications
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Long Chain Fatty Acid Oxidation Disorder
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Lysosomal Acid Lipase Deficiency
Wilson Disease
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ANCA-Associated Vasculitis
Cold Agglutinin Disease
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Duchenne Muscular Dystrophy
Friedreich Ataxia
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Lennox-Gastaut Syndrome
Multiple Sclerosis
Myasthenia Gravis
Neuromyelitis Optica Spectrum Disorder
Spinal Muscular Atrophy
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