In this episode of the Rare Care podcast, Larry Luxner, senior correspondent for Rare Disease Advisor, interviews researcher Adrian Krainer, PhD, from the Cold Spring Harbor Laboratory in New York. Dr. Krainer perfected the RNA splicing technique that led to the development of nusinersen, the first treatment for spinal muscular atrophy.

Read the full story: The Brains Behind Nusinersen: A Visit With Geneticist Adrian Krainer, PhD