Which of the statements below about the therapies for Pompe disease are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about Pompe disease gene therapy. References A gene transfer study for late-onset Pompe…
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Peter Saltonstall, president and CEO of the National Organization for Rare Disorders (NORD), about the 40th anniversary of the landmark Orphan Drug Act. Read the full story here: At 40, Orphan Drug Act Enjoys Rare Bipartisan Support
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Philip J. Brooks, PhD, acting director of the Division of Rare Diseases Research Innovation at the National Institutes of Health’s National Center for Advancing Translational Sciences.
Which of the statements below about the histology of Pompe disease are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Good luck! Read more about Pompe disease histology.
Which of the statements below about the comorbidities of Pompe disease (PD) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about Pompe disease comorbidities.
Which of the statements below about life expectancy in Pompe disease are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about life expectancy in Pompe disease.
Test your knowledge about the differential diagnosis of Pompe disease with this short quiz and see how you compare to others.
Which of the statements below about late-onset Pompe disease (PD) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about Pompe types.
Which of the statements below about the diet for Pompe disease (PD) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about Pompe disease patient education.
Which of the statements below about the risk factors of Pompe disease (PD) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about Pompe disease risk factors
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