PNH Podcasts

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An Interview With Abigail Jenkins, President and CEO of Gamida Cell

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Abigail Jenkins, president and CEO of Gamida Cell, on the company’s development of omidubicel as an alternative to umbilical cord blood in stem cell transplants for myelofibrosis and other diseases. Read the full story here: Omidubicel Shows Promise as Replacement for Umbilical Cord Blood in Stem…

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Test Your Knowledge About Therapies for PNH

Which of the statements below about the therapies for paroxysmal nocturnal hemoglobinuria (PNH) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about PNH therapies.

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An Interview With PJ Brooks, PhD, on the Bespoke Gene Therapy Consortium

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Philip J. Brooks, PhD, acting director of the Division of Rare Diseases Research Innovation at the National Institutes of Health’s National Center for Advancing Translational Sciences.

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