LAL-D Podcasts Archives

An Interview With Abigail Jenkins, President and CEO of Gamida Cell

January 25, 2023

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Abigail Jenkins, president and CEO of Gamida Cell, on the company’s development of omidubicel as an alternative to umbilical cord blood in stem cell transplants for myelofibrosis and other diseases. Read the full story here: Omidubicel Shows Promise as Replacement for Umbilical Cord Blood in Stem…

CAD Podcasts, CCA Podcasts, CF Podcasts, HAE Podcasts, HEM Podcasts, LAL-D Podcasts, LCFAOD Podcasts, Podcasts, POMPE Podcasts

An Interview With Peter Saltonstall, President and CEO of NORD

January 18, 2023

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Peter Saltonstall, president and CEO of the National Organization for Rare Disorders (NORD), about the 40th anniversary of the landmark Orphan Drug Act. Read the full story here: At 40, Orphan Drug Act Enjoys Rare Bipartisan Support

LAL-D Podcasts, LAL-D Quizzes, Quizzes, Uncategorized

Test Your Knowledge About the Guidelines for LAL-D

January 6, 2023

Which of the statements below about the guidelines for lysosomal acid lipase deficiency (LAL-D) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about LAL-D guidelines.

LAL-D Podcasts, LAL-D Quizzes, Quizzes, Uncategorized

Test Your Knowledge of Enzyme Replacement Therapy for LAL-D

December 12, 2022

Which of the following is untrue regarding sebelipase alfa therapy for lysosomal acid lipase deficiency? Select an option for the question, then submit your answer to see your score and the average score for everyone who has taken the quiz. Read more about therapies for lysosomal acid lipase deficiency.

LAL-D News Briefs, LAL-D Podcasts, News Briefs, Podcasts, Pompe News Briefs, WD Podcasts

An Interview With Annie Kennedy of the EveryLife Foundation for Rare Diseases

November 21, 2022

Rare Disease Advisor’s Larry Luxner interviews Annie Kennedy, EveryLife Foundation for Rare Diseases’ head of policy, advocacy, and patient engagement.

LAL-D Podcasts, LAL-D Quizzes, Quizzes, Uncategorized

Test Your Knowledge About LAL-D Comorbidities

November 14, 2022

Which of the statements below about the comorbidities of lysosomal acid lipase deficiency (LAL-D) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about LAL-D comorbidities.

LAL-D Podcasts, LAL-D Quizzes, Quizzes, Uncategorized

Test Your Knowledge About LAL-D Therapies

October 24, 2022

Which of the statements below about the therapies for lysosomal acid lipase deficiency (LAL-D) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about the therapies of LAL-D.

Lysosomal Acid Lipase Deficiency Differential Diagnosis

LAL-D Podcasts, LAL-D Quizzes, Quizzes

Test Your Knowledge About the Diagnosis of LAL-D

September 19, 2022

Which of the statements below about LAL-D diagnosis are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about LAL-D here.

LAL-D Podcasts, LAL-D Quizzes, Quizzes

Test Your Knowledge About the Symptoms of LAL-D

August 9, 2022

Which of the statements below about the symptoms of lysosomal acid lipase deficiency (LAL-D) is correct? Select one of the options, then submit your answer to see your score and the average score for everyone who has taken the quiz. Read more about the symptoms of LAL-D.

LAL-D Podcasts, LAL-D Quizzes, Quizzes

Test Your Knowledge of Patient Education in LAL-D

July 25, 2022

Patient education promotes an understanding of a condition and available treatment options. Take our quiz on patient education for LAL-D.

LAL-D Podcasts

Want to read more?