HEM Podcasts Archives

FA News Briefs, FA Podcasts, hATTR News Briefs, hATTR Podcasts, HEM News Briefs, HEM Podcasts, PNH News Briefs, PNH Podcasts, SCD News Briefs, SCD Podcasts, SM News Briefs, SM Podcasts

Dr. Federico Stella on Using Nonrestrictive Diets After Stem Cell Transplantation

March 15, 2023

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Federico Stella, MD, on the controversial practice of severely restricting the diets of patients who have just undergone stem cell transplants. Read the full story here: Italian Hematologist Urges End to ‘Useless’ Restrictive Diets After Stem Cell Transplants

HEM News Briefs, HEM Podcasts, Podcasts

An Interview With Darlene Shelton, Founder and President of Danny’s Dose Alliance

February 22, 2023

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Darlene Shelton, founder and president of Danny’s Dose Alliance, a Missouri-based nonprofit that seeks to ensure proper emergency medical care for all patients with hemophilia and other bleeding disorders. Read the full story here: Danny’s Dose Alliance Fights for Proper Emergency Care for Those With Bleeding…

CAD Podcasts, CCA Podcasts, CF Podcasts, HAE Podcasts, HEM Podcasts, LAL-D Podcasts, LCFAOD Podcasts, Podcasts, POMPE Podcasts

An Interview With Peter Saltonstall, President and CEO of NORD

January 18, 2023

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Peter Saltonstall, president and CEO of the National Organization for Rare Disorders (NORD), about the 40th anniversary of the landmark Orphan Drug Act. Read the full story here: At 40, Orphan Drug Act Enjoys Rare Bipartisan Support

DLBCL Podcasts, hATTR Podcasts, HEM Podcasts, MG Podcasts, PAH Podcasts, PNH Podcasts, Podcasts, POMPE Podcasts, SM Podcasts, WD Podcasts

An Interview With PJ Brooks, PhD, on the Bespoke Gene Therapy Consortium

December 29, 2022

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Philip J. Brooks, PhD, acting director of the Division of Rare Diseases Research Innovation at the National Institutes of Health’s National Center for Advancing Translational Sciences.

HEM Podcasts, HEM Quizzes, Quizzes, Uncategorized

Test Your Knowledge About the Etiology of Hemophilia

September 9, 2022

Which of the statements below about the etiology of hemophilia are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about hemophilia etiology.

HEM Podcasts, HEM Quizzes

Test Your Knowledge About the History of Hemophilia

August 22, 2022

Which of the statements below about the history of hemophilia? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about the history of hemophilia here.

HEM Podcasts, HEM Quizzes, Quizzes

Test Your Knowledge About the Symptoms of Hemophilia

February 9, 2022

Take our quick quiz on the symptoms of hemophilia and see how your score compares to the average score of others who have taken the quiz.

HEM Podcasts, Podcasts, Uncategorized

The Pursuit of Redosable Gene Therapies for Hemophilia With Dr. Doug Kerr

By

Larry Luxner

September 24, 2021

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Doug Kerr, MD, PhD, chief medical officer at Generation Bio in Cambridge, Massachusetts. The company is aggressively pursuing redosable gene therapies for hemophilia and other rare diseases. Read the full article: Generation Bio Pursues Redosable Gene Therapy for Hemophilia A

HEM Podcasts