Which of the statements below about the epidemiology of Duchenne muscular dystrophy (DMD) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about DMD epidemiology. References Theadom T, Rodrigues M, Roxburgh R, et…
Which of the statements below about the prognosis of Duchenne muscular dystrophy (DMD) is correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about the prognosis of DMD.
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Brenda Wong, MD, an expert on Duchenne muscular dystrophy (DMD) and director of the MDA Care Center at the University of Massachusetts Chan Medical School in Worcester. Read the full story here: MDA Honors 2 Massachusetts Researchers for Groundbreaking Work in Duchenne
Which of the statements below about the differential diagnosis of Duchenne muscular dystrophy (DMD) are correct? Select one of the options for each question, then submit your answers to see your score and the average score for everyone who has taken the quiz. Read more about DMD differential diagnosis.
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Jennifer Wallace Valdes, PT, founder of the Duchenne Therapy Network and physical therapist with CureDuchenne, on the importance of physical therapy and exercise in boys and young men with Duchenne muscular dystrophy. Read the full story here: New Mexico Mom’s Big Challenge: Raising Identical Twin Boys…
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Deanna Tucker, PharmD, a medical science liaison team leader at Sarepta Therapeutics, on the company’s efforts to develop a gene therapy for Duchenne muscular dystrophy. Read the full story here: Sarepta Simultaneously Pursues Exon Skipping, PPMO, and Gene Therapies for DMD
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Michael Kelly, PhD, chief scientific officer at CureDuchenne, on the latest developments in exon skipping, gene therapy, and other treatments for Duchenne muscular dystrophy. Read the full story here: Gene Therapy Could Emerge as a DMD Treatment in 2023
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Paul Heaton, a Montana cattle rancher whose son has Duchenne muscular dystrophy (DMD), on his Calves2Cure DMD fundraising initiative. Read the full story here: A Unique Way Raise Money for DMD Research: Cattle Auctions
Which of the statements below about the cause of Duchenne muscular dystrophy is correct? Select one of the options, then submit your answer to see your score and the average score for everyone who has taken the quiz. Read more about Duchenne muscular dystrophy etiology here.
Rare Disease Advisor senior correspondent Larry Luxner interviews Pradeep Mammen, MD, director of the UT Southwestern Neuromuscular Cardiomyopathy Clinic.
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