Podcasts

Durhane Wong-Rieger

Dr. Durhane Wong-Rieger on the Challenges Faced by Rare Disease Patients in Canada

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Durhane Wong-Rieger, PhD, president and CEO of the Canadian Organization for Rare Disorders (CORD) and chair of Rare Diseases International (RDI). Dr. Wong-Rieger talks about the challenges of diagnosing and treating diseases in Canada, as well as advancing access to therapies around the globe. Read the…

Rare Care podcast logo

An Update on LAL-D With Dr. Paul Martin of Nationwide Children’s Hospital

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Paul T. Martin, PhD, principal investigator at the Center for Gene Therapy at Nationwide Children’s Hospital in Columbus, Ohio. Dr. Martin has been at the forefront of research into potential gene therapies for lysosomal acid lipase deficiency, or LAL-D. Read the full article: Gene Therapy May…

Rare Care podcast logo

The Pursuit of Redosable Gene Therapies for Hemophilia With Dr. Doug Kerr

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Doug Kerr, MD, PhD, chief medical officer at Generation Bio in Cambridge, Massachusetts. The company is aggressively pursuing redosable gene therapies for hemophilia and other rare diseases. Read the full article: Generation Bio Pursues Redosable Gene Therapy for Hemophilia A

Rare Care podcast logo

Perspectives on Long Chain Fatty Acid Oxidation Disorder With Dr. Jerry Vockley

Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Jerry Vockley, MD, PhD, chief of medical genetics at Pennsylvania’s UPMC Children’s Hospital of Pittsburgh. Dr. Vockley is also the founder of INFORM, the International Network for Fatty Acid Oxidation Research and Management, which will hold its next annual conference virtually October 27-28, 2021. Read the…

Next hm-quiz in AATD Quizzes