Latest News
Infusion Ports Show Reliable Central Venous Access for Pediatrics With SCD
Children With SCD May Face Increased Nutritional Challenges
Deferiprone Provides a New Treatment Option for SCD
TALEN-Based Process Leads to Gene Correction in SCD Cells
Phase 1 Trial Results Suggest Possible Functional Cure for Sickle Cell Disease
First Patient Enrolled in CEDAR Clinical Trial for Sickle Cell Disease
Newly Developed Multiplex Network Could Improve Rare Disease Research
Gene Therapeutics Could Benefit Many Patients With Rare Diseases
The Hurdles of Genetic Testing for the Rare Disease Community
SCD Clinical Trials
Features
An Often Overlooked Disease Exiting the Shadows
Funding for sickle cell disease clinical trials and drug development has steadily increased and groundbreaking gene therapy research is being conducted.
Using Technology to Boost Ethnic, Geographic Diversity in Clinical Trials
Eliminating geographic and ethnic bias in clinical trials for rare diseases is the goal of Jeeva Informatics, says founder and CEO Harsha K. Rajasimha, PhD.
CORD Aims to Improve Diagnosis, Drug Access for Canada’s Rare Disease Patients
The Canadian Organization for Rare Disorders advocates for better diagnosis and drug access for Canada’s 3 million people with rare diseases.
Newborn Screening Saves Lives, Yet Raises Some Ethical Issues, Expert Says
Georgianne Arnold, MD, an expert on newborn screening, says the practice clearly saves lives, yet raises ethical concerns.
Insights
Carrier Screening for Autosomal Recessive and X-Linked Conditions
A study published in Genetics In Medicine sought to develop and answer a series of questions regarding the process of screening for carriers of a disease.
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