Latest News
Gene Editing Demonstrates Efficacy in Sickle Cell Disease via Optical Test
Buprenorphine Shows Promise as Safe Alternative to Other Opioids for Pain in SCD
Sickle Cell Disease May Triple the Risk of Preterm Birth
Risk Factors, Mitigation Strategies, and Management Recommendations in SCD
Gallbladder Disease Associated With Age and Disease Severity in Children With SCD
New Study to Test Safety and Efficacy of a Cannabinoid in Sickle Cell Disease
Study Suggests New Method of Preventing Vaso-Occlusive Crises in Sickle Cell Disease
Rare Disease Patients and Advocate to Headline NORD Conference in October
First Patient Dosed With Graphite Bio’s Gene-Editing Therapy for SCD
SCD Clinical Trials
Insights
ST-Segment Elevation Myocardial Infarction: A Potential Complication of SCD
Epidemiological studies reveal that cardiovascular disease is a leading cause of death around the world. Specifically, the prevalence of ST-segment elevation myocardial infarction (STEMI) has steadily increased in recent years. Acute coronary syndrome (ACS), which encompasses STEMI, is one of the potential complications of sickle cell disease. It is often fatal. Cardiovascular disease represents a…
The Parallels Between Sickle Cell Disease and Accelerated Aging
Aging is a process we all go through. On one hand, aging is a good parameter of health, since it requires one to survive into late adulthood. In fact, many countries are worried that their populations are aging too well and that soon there will be more individuals who have retired than there are those…
Understanding Infertility in Patients With Sickle Cell Disease
Fertility and female reproductive rights have become hot-button issues in recent years. While the problem of infertility has been around since antiquity, we now possess new ways of treating infertility that were previously unthinkable, such as in vitro fertilization, freezing of the eggs and sperm, and surrogacy. The new spectrum of therapeutic options to treat…
Techniques for Detecting and Monitoring Sickle Cell Disease
Various diagnostic techniques for sickle cell disease are in play and others are being refined for future use.
Are Sickle Cell Carriers at Higher Risk of Developing Health Complications?
We explore the controversy around whether sickle cell carriers are at a higher risk of developing health complications.
The Confluence of Challenges in Fighting Sickle Cell Disease in the Congo
In countries such as the Democratic Republic of Congo, the fight against sickle cell disease takes up significant healthcare resources.
SCD Features
The Alliance for Regenerative Medicine Fights for Better Cell, Gene Therapies
The Alliance for Regenerative Medicine aims to help in the development of safe and effective regenerative therapies that can benefit rare disease patients.
‘Fundamental Flaws’ Plague Drug Development Process, Ultragenyx CEO Dr. Emil Kakkis Says
Ultragenyx CEO Dr. Emil D. Kakkis said federal regulators should focus more on biomarkers and less on clinical endpoints when it comes to drug approvals.
L-Glutamine in Sickle Cell Disease: The Real-World Impact to Date
L-glutamine was approved in 2017 to treat acute complications in patients with sickle cell disease, but uptake of and adherence to it have been limited.
An Often Overlooked Disease Exiting the Shadows
Funding for sickle cell disease clinical trials and drug development has steadily increased and groundbreaking gene therapy research is being conducted.
Using Technology to Boost Ethnic, Geographic Diversity in Clinical Trials
Eliminating geographic and ethnic bias in clinical trials for rare diseases is the goal of Jeeva Informatics, says founder and CEO Harsha K. Rajasimha, PhD.
CORD Aims to Improve Diagnosis, Drug Access for Canada’s Rare Disease Patients
The Canadian Organization for Rare Disorders advocates for better diagnosis and drug access for Canada’s 3 million people with rare diseases.
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