Latest News
New Study Set to Assess Mim8 Therapy in People With Hemophilia A
Distress Associated With Poor Adherence to Hemophilia Prophylaxis
Delphi Consensus Study Highlights Gaps in Knowledge of Synovitis in Hemophilia
Pain Affects Quality of Life in Men With Hemophilia, Regardless of Disease Severity
Expert Opinion: Intra-articular PRP Injections Not Appropriate for Patients With Hemophilia
Study Supports the Use of BAY 81-8973 for Hemophilia A Prophylaxis and Treatment
Valoctocogene Roxaparvovec Offers Stable and Durable Bleed Control in Hemophilia A
Top-Line Results Released From Hemophilia B Study of Fidanacogene Elaparvovec
Myofascial Therapy an Effective Intervention in Patients With Hemophilic Arthropathy
Latest Clinical Trials
Insights
The Dangers of Delayed Diagnosis in Acquired Hemophilia A
Excessive bleeding in patients with undiagnosed acquired hemophilia A can be lethal.
Managing Mild Hemophilia in Clinical Practice
Patients with nonsevere hemophilia should still be managed effectively to prevent a deterioration in their quality of life.
Putting Patients First in Hemophilia Treatment Decision Making
Patients should be placed front and center in any discussions about hemophilia therapeutic options.
Could Immunotherapy Reduce Inhibitor Formation in Patients With Hemophilia A?
Scientists suggest immunosuppression therapy may help reduce formation of inhibitors with factor VIII replacement therapy in hemophilia.
Ensuring Sexual Health in Patients With Hemophilia
Although often overlooked, sexual dysfunction can occur in patients with hemophilia, negatively impacting quality of life.
How Hemophilia Continues to Affect Patients’ Quality of Life
Questionnaires assessing the quality of life of patients with hemophilia reveal that a large percentage of individuals struggle on a daily basis.
Strategies for Managing Inhibitor Development in Hemophilia
The mainstay of hemophilia treatment is impeded by a stubborn problem that can sometimes drastically reduce its efficacy.
Using Thrombin Generation Assays to Monitor the Effects of Hemophilia A Therapy
Research shows thrombin generation assays can monitor the efficacy of hemophilia A treatment in a way that the mere monitoring of plasma FVIII activity cannot.
Hemophilia Features
At 40, Orphan Drug Act Enjoys Rare Bipartisan Support
Rare disease advocates are marking the 40th anniversary of the landmark Orphan Drug Act, which has led to over 1100 approvals for new therapies.
Ambitious NCATS Bespoke Gene Therapy Consortium Targets Ultrarare Diseases
The Bespoke Gene Therapy Consortium (BGTC) is an ambitious public-private partnership that aims to develop gene therapies for ultrarare diseases.
The Alliance for Regenerative Medicine Fights for Better Cell, Gene Therapies
The Alliance for Regenerative Medicine aims to help in the development of safe and effective regenerative therapies that can benefit rare disease patients.
Hemophilia May Benefit From Redosable Gene Therapy
Generation Bio is working to “create the next generation of gene therapy” that will enable the redosable, durable expression of missing proteins.
Rare Care Podcast
The Pursuit of Redosable Gene Therapies for Hemophilia with Dr. Doug Kerr
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