MG Clinical Trials Rare Care Podcast
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Hemophilia
Latest Clinical Trials Rare Care Podcast The Pursuit of Redosable Gene Therapies for Hemophilia with Dr. Doug Kerr
Pompe Disease
Latest Clinical Trials Pompe Disease Clinical Insights Rare Care Podcast Barry Byrne, MD, director of the University of Florida’s Powell Gene Therapy Center in Gainesville, has spent years researching potential gene therapies for Pompe disease. In this edition of the Rare Care podcast, Dr. Byrne comments on the FDA’s recent approval of avalglucosidase alfa-ngpt (Nexviazyme)…
Long Chain Fatty Acid Oxidation Disorder
Latest Clinical Trials Rare Care Podcast Perspectives on Long Chain Fatty Oxidation Disorder With Dr. Jerry Vockley
Lysosomal Acid Lipase Deficiency
Latest Clinical Trials Rare Care Podcast An Update on LAL-D With Dr. Paul Martin of Nationwide Children’s Hospital
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