Gamida Cell is gearing up to begin sales of omidubicel from Israel to US hospitals for use in stem cell transplants, pending FDA approval of the therapy.
The Alliance for Regenerative Medicine aims to help in the development of safe and effective regenerative therapies that can benefit rare disease patients.
Dr. Haggi Mazeh, chief of surgery at one of Israel’s top hospitals, discusses diagnosing and treating medullary thyroid carcinoma.
MTC “can get aggressive and nasty” but it is not necessarily a death sentence, said surgical oncologist David Goldenberg, MD, FACS, author of a new book.
In late February 2016, while getting dressed for work, George Labonte — the deputy police chief of Wrentham, Massachusetts — noticed a lump under his Adam’s apple as he knotted the tie of his uniform. Labonte’s primary care provider ordered imaging and referred the 35-year-old to an ear, nose, and throat specialist. A biopsy showed…
Under COVID-19’s lingering shadow, the National Organization of Rare Disorders (NORD) has presented its 2021 Rare Impact Awards to 24 pharmaceutical firms, researchers, politicians, and nonprofit groups for their efforts over the past year on behalf of patients with such illnesses.
As the super-contagious Delta variant of COVID-19 sweeps across the globe, driving up infection rates as well as deaths, top US health officials are urging everyone 12 and older—including the country’s 30 million or so rare disease patients—to get vaccinated quickly.
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