Gamida Cell is gearing up to begin sales of omidubicel from Israel to US hospitals for use in stem cell transplants, pending FDA approval of the therapy.
Dr. Rahul Banerjee of the University of Washington discusses the benefits and drawbacks of using synthetic control arms in randomized controlled trials.
The Alliance for Regenerative Medicine aims to help in the development of safe and effective regenerative therapies that can benefit rare disease patients.
Mind, Mood and Memory: The Neurobehavioral Consequences of Multiple Sclerosis explains the potential benefits of cognitive rehabilitation in people with MS.
The Canadian Organization for Rare Disorders advocates for better diagnosis and drug access for Canada’s 3 million people with rare diseases.
Multiple sclerosis (MS) is the most common immune-mediated demyelinating disease of the central nervous system (CNS). It is also characterized by inflammation and axonal degeneration in the CNS and is vastly heterogeneous in its presentation.1 Diagnosis of MS has improved over time; however, there is still room for improvement: the mean time from first medical…
CAESAREA, Israel — Multiple sclerosis survivor Michael Faibisch, 59, clearly remembers the day in August 2003 when his symptoms began. The Maryland native, who’s lived in Israel since 1979, had started long-distance bicycling a year earlier to get back in shape. At the time, he weighed 130 kilograms (287 pounds) and was an emotional wreck. “I…
As the super-contagious Delta variant of COVID-19 sweeps across the globe, driving up infection rates as well as deaths, top US health officials are urging everyone 12 and older—including the country’s 30 million or so rare disease patients—to get vaccinated quickly.
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