ANCA Features, CAD Features, CCA Features, CF Features, Features, HAE Features, hATTR Features, HEM Features, IPF Features, LAL-D Features, LCFAOD Features, PNH Features, Pompe Features, SCD Features
At 40, Orphan Drug Act Enjoys Rare Bipartisan Support
Rare disease advocates are marking the 40th anniversary of the landmark Orphan Drug Act, which has led to over 1100 approvals for new therapies.