Ilan Ganot, CEO of Solid Biosciences, cofounded the company with his wife, Annie, after their son, Eytani, was diagnosed with Duchenne in 2012.
Jerry R. Mendell, MD, professor of neurology and pediatrics at Nationwide Children’s Hospital has devoted his life’s work to curing DMD.
A video of Jordan McLinn, who has DMD, went viral when he tried to embrace then-President Trump before he signed the “Right to Try” bill at the White House.
Jay Griffin, whose son Franklin has DMD, knows all too well what it’s like to be a member of a minority group and in search of help with a rare disease.
Courtney Young, PhD, developed her startup, MyoGene Bio, to find a cure for Duchenne muscular dystrophy, which plagues her young cousin.
Pilot programs in New York, Massachusetts, and North Carolina testing babies for DMD may bolster the case for nationwide screening for this rare disease.
Duchenne muscular dystrophy (DMD) and spinal muscular atrophy (SMA) will take center stage at the first in-person annual gathering of the Muscular Dystrophy Association (MDA) since March 2019.
Families of boys with Duchenne muscular dystrophy have a hard time accessing lifesaving therapies and services in Ukraine, Europe’s poorest country.
This year’s CureDuchenne Futures conference features a panel on exon skipping as well as sessions on the family’s role in research, quality of life, cognition in Duchenne, and defining happiness.
When it comes to rare disorders, Israel—a New Jersey-sized nation of 9.3 million that’s made headlines this year for its highly successful coronavirus vaccination campaign—is clearly an emerging powerhouse.