CureDuchenne FUTURES National Conference 2021

Complete Coverage


Gene Therapy Offers Promise in Treating Duchenne, Along with Significant Obstacles

By 2025, between 10 and 20 new gene therapies could win approval annually by the US Food and Drug Administration (FDA), most of them delivered via adeno-associated virus (AAV).  Yet Duchenne muscular dystrophy (DMD) presents some unique challenges for AAV-delivered gene therapy — namely because the dystrophin gene, which is missing in DMD, is one of…

Rare Disease Advisor is excited to cover CureDuchenne’s 2021 FUTURES Nationals Conference. The CureDuchenne 2021 FUTURES National Conference is a virtual event focused on bringing education, resources, and connection to the Duchenne community in a family-friendly environment. This year’s conference agenda and special events will focus on Quality of Life. CureDuchenne will be offering multiple robust presentations and panel discussions, a Symposium, a Resource Fair, e-Gaming experiences, and more.

For registration and program info, visit the FUTURES 2021 info page.

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