WODC 2022

News & Features

WODC 2022

US and European Drugmakers, Regulators Face Common Rare Disease Challenges

By

Larry Luxner

Publish Date July 15, 2022

Incentives for research, speeding diagnosis, and access to therapies are the most significant challenges in rare disease, US and European experts said.

WODC 2022

Cell, Gene Therapy Breakthroughs Outpacing Healthcare System, Experts Say

By

Larry Luxner

Publish Date July 15, 2022

The US healthcare system cannot keep up with the rapidly advancing field of gene therapy, experts who spoke at the 2022 World Orphan Drug Congress said.

WODC 2022

Rare Disease Advocates: In COVID’s Aftermath, ‘Build Back Smarter’

By

Larry Luxner

Publish Date July 14, 2022

The COVID-19 pandemic and its effect on rare disease patients worldwide offers valuable lessons for the future, World Orphan Drug Congress panelists said.

WODC 2022

Reconsidering the Role of Disease Biomarkers in Drug Development

By

Terri Airov

Publish Date July 13, 2022

Using primary disease biomarkers as endpoints for drug approvals could transform the development of rare disease treatments, Emil Kakkis, MD, PhD, said.

Rare Disease Advisor is proud to attend the 2022 World Orphan Drug Congress, which is being held July 11-13, 2022, in Boston. Stay tuned to RDA as we offer live coverage of the event, plus expanded coverage featuring exclusive stories and interviews with rare disease leaders and influencers.